Imagine hearing the words: "Your child has a genetic disease that is likely to be fatal." For parents of infants diagnosed with Spinal Muscular Atrophy (SMA) Type 1 , this was once a devastating and hopeless reality. But today, a revolutionary treatment is rewriting that story. Its name is Zolgensma (onasemnogene abeparvovec-xioi) , and it’s not just a drug—it’s a one-time gene therapy offering a chance at a future. But what exactly is this "miracle" drug, how does it work, a

For those living with progressive blindness due to a specific genetic mutation, a life in the dark was the only future. Enter Luxturna—the first-ever directly administered gene therapy that can restore functional vision. Discover the science behind this medical marvel and the stories of hope it's creating for patients and families.